Gene therapy using modified blood stem cells helped five adults with severe hemophilia A reach therapeutic levels of clotting ...

After having a bad experience getting three vaccines at once, columnist Jennifer Lynne says that next time, she'll space them apart.

Columnist Joe MacDonald, who'll soon move to a new city, appreciates the care from his therapist to treat his "hemophilia dad" anxieties.

Metagenomi says it hopes to start clinical trials next year to test MGX-001, its gene-editing therapy candidate for ...

For the first time in Denmark, people with hemophilia B have been treated with the gene therapy Hemgenix (etranacogene ...

Hummingbirds offer an example to help understand people like Caeleb, who are classified as ambulatory wheelchair users. While these birds soar through the air gracefully and quickly, they must also ...

With a touch of humor about the "hot news," columnist Alliah Czarielle's husband handles the dramatic consequences of a ...

Rev. Dr. Joe K. MacDonald is a pastor in the New Mexico Annual Conference of the United Methodist Church. He and his wife, Cazandra, live in Belen, New Mexico, along with their youngest son, Caeleb, ...

Be Biopharma has raised $92 million to support the first-in-human Phase 1/2 trial of BE-101, which is made to lower bleeding ...

Small vesicles in the saliva of people with severe hemophilia A may explain why these patients rarely have bleeds in their mouth and throat. The vesicles contain a protein complex that’s able to ...

Hemophilia is a rare disorder in which a person’s blood is not able to clot properly, resulting in unusually easy and prolonged bleeding. Within the blood, proteins called clotting factors normally ...

I hate it when the term “hero” is used to describe me and my daily life with hemophilia. Honestly, I despise it being used to describe anyone living with a rare disease or disability. I think it’s the ...