NHS patients with sickle cell disease will be able to benefit from a groundbreaking gene-editing treatment that offers the prospect of a cure for the condition. The one-off gene therapy, known as ...

Read about exa-cel being rolled out on the NHS, providing a 'functional cure' for some patients with severe sickle cell ...

NHS officials estimate around 50 people a year will receive treatment now it has been approved for use for certain patients with severe sickle cell disease. | ITV National News ...

Everything you need to know about agonising sickle cell disease and the ‘revolutionary’ new DNA therapy that's being rolled ...

Abnormal cells can clog blood vessels, leading to severe pain episodes and restricting oxygen delivery to vital organs ...

Base editing utilizes enzymes to modify single amino acids at the most foundational unit of DNA, called a base.

Sickle cell disease impacts more than 100,000 people in the United States. It’s estimated that more than two million ...

WINSTON-SALEM, N.C. — Emory Moore, a 12-year-old treated at Brenner Children’s Hospital for sickle cell disease, received a ...

The UK has approximately 17,500 individuals living with sickle cell disease, a condition particularly prevalent amongst those ...

We can do better. We can build a system that provides coordinated high-quality care to every patient who needs it.

A £1.65 million treatment has been approved for use for some NHS patients, offering hope of a cure to those with an inherited ...