It is the first pivotal trial of a mutation-agnostic RP gene therapy and the only study to show a 0.3 or better LogMAR improvement in retinal degenerative disease, according to Nanoscope.

Financial writer discusses MGX's gene editing technology, cash runway, and lack of clinical data for potential future ...

New research uncovers how declining protein clearance mechanisms with age lead to Alzheimer’s, Parkinson’s, and other ...

This case study explores a rare overlap of hidradenitis suppurativa and porokeratosis, as well as highlights the unique ...

Learn about cystic fibrosis, a genetic disorder that affects ... CF — including those with rare and nonsense mutations — and pursuing daring, new opportunities to one day develop a lifelong cure.

Do you have blue eyes? We talked to experts to discover curious facts about baby blues, including whether your biological family is bigger than you ever imagined.

The rationale is that MCO can restore the light-detecting function of retinal cells that are damaged in RP, regardless of the underlying mutation ... gene therapy’s favourable safety profile ...

We were especially curious about the echocardiogram results which would reveal how well Johnny's then-19-year-old prosthetic heart valve was functioning. Thankfully, his valve was in good working ...

Daily low-dose aspirin can help prevent cancers from returning in about a third of colon cancer patients, a new study says.

Elicio Therapeutics, Inc.’s ELTX share price has surged by 13.41%, which has investors questioning if this is right time to ...

Low-dose aspirin significantly reduced risk for colorectal cancer recurrence among patients with mutations in the PI3K ...

The superfamily 1 (SF1) and SF2 enzymes are non-hexameric enzymes possessing both helicase and single-stranded DNA (ssDNA) translocase activities, as well as the ability to displace proteins from DNA.