Read about exa-cel being rolled out on the NHS, providing a 'functional cure' for some patients with severe sickle cell ...
NHS patients with sickle cell disease will be able to benefit from a groundbreaking gene-editing treatment that offers the prospect of a cure for the condition. The one-off gene therapy, known as ...
NHS officials estimate around 50 people a year will receive treatment now it has been approved for use for certain patients with severe sickle cell disease. | ITV National News ...
Everything you need to know about agonising sickle cell disease and the ‘revolutionary’ new DNA therapy that's being rolled ...
Abnormal cells can clog blood vessels, leading to severe pain episodes and restricting oxygen delivery to vital organs ...
Base editing utilizes enzymes to modify single amino acids at the most foundational unit of DNA, called a base.
Sickle cell disease can be managed, but many children in Africa lack access to such treatment. As a result, four of five African children born with the disorder die before age 5, according to the ...
Sickle cell disease impacts more than 100,000 people in the United States. It’s estimated that more than two million ...
WINSTON-SALEM, N.C. — Emory Moore, a 12-year-old treated at Brenner Children’s Hospital for sickle cell disease, received a ...
After moving from Sierra Leone to London, guest columnist Richard Bayliss received a proper diagnosis and care plan for his sickle cell.