0:53 UBC researchers report breakthrough in Huntington treatment Scientists are unravelling the mystery of what triggers Huntington’s disease, a devastating and fatal hereditary disorder that ...

DMD is a rare neuromuscular disease caused by a mutation in the DMD gene, which encodes a protein called dystrophin that is essential for muscle health. Vamolorone is a synthetic corticosteroid ...

Santhera’s Agamree is indicated for patients aged four years and older with Duchenne muscular dystrophy (DMD). Credit: JohnnyGreig via Getty Images. Swiss biotech Santhera Pharmaceuticals has started ...

An organic disease is one in which there is a measurable change to tissues, organs, or body systems. A functional disease is one in which there are abnormal symptoms or changes in function but with no ...

The study leaders share their findings and what makes them compelling and meaningful. Video: Broad Institute of MIT and Harvard At a glance: Study explains long-standing question of why Huntington’s ...

Pubali Bank PLC has promoted Sultana Sarifun Nahar to the post of deputy managing director (DMD). Nahar is the first woman to hold this position, marking a significant milestone in the history of ...

What Is Duchenne Muscular Dystrophy? Muscular dystrophies are a group of diseases that make muscles weaker and less flexible over time. Duchenne muscular dystrophy (DMD) is the most common type.

INS1201 represents the first application of Insmed’s targeted AAV delivery platform in DMD. Credit: JHVEPhoto / Shutterstock ... This platform enables the delivery of larger genes, which could unlock ...

Histone deacetylase inhibitor. Givinostat (Duvyzat) is the first non-steroid drug approved to treat people with all genetic variations of DMD. It delays the disease's progression by targeting an ...

Today, the Governments of Canada and the province of New Brunswick signed the National Strategy for Drugs for Rare Disease (DRD) agreement to invest over $32 million over three years to improve access ...

According to Nation's Restaurant News (NRN), Florida-based franchisee DMD Ventures, which operates businesses such as Twin Peaks, Papa Johns and Candlewood Suites, among others, has filed for ...

Altruism values for treatments of rare, severe pediatric diseases have not been estimated. This study found the altruism value for a hypothetical new Duchenne muscular dystrophy treatment to be $ ...