Discover the importance of vision, genetic eye disorders, and RNA-based therapies for precision treatment in India and ...

The NCCN's new resource educates patients on genetic testing for hereditary cancer risk, focusing on breast, ovarian, pancreatic, and prostate cancers. Advances in genetic technology, spurred by ...

UnitedHealth Group reported a medical care ratio in 2024 of 85.5% compared with 83.2% in 2023. In 2024, UnitedHealth Group saw full year revenue grow 8% over 2023 to reach $400.3 billion. Adjusted ...

Will the Stelara biosimilars be a reprise of the Humira biosimilars in 2023 and be slow to catch on? Biosimilar watchers circled 2023 as a red-letter year because that was the year that the Humira ...

INS1201 represents the first application of Insmed’s targeted AAV delivery platform in DMD. Credit: JHVEPhoto / Shutterstock. Duchenne muscular dystrophy (DMD) is a rare genetic disorder that is ...

Duchenne muscular dystrophy (DMD) is the most common type. It’s caused by flaws in the gene that controls how the body keeps muscles healthy. The disease almost always affects boys, and symptoms ...

In 1986, researchers discovered the gene that, when defective or flawed, causes Duchenne muscular dystrophy. In 1987, the muscle protein associated with this gene was named dystrophin. Duchenne ...

The inspector general’s office has two main recommendations to improve the accelerated approvals process. The FDA agreed with the watchdog that meetings with sponsors need to be better documented and ...

an investigational therapy for Duchenne muscular dystrophy (DMD), and is still ongoing in the United Kingdom. The most-read gene therapy articles included topics on FDA approvals, chimeric antigen ...

“At Alloy Therapeutics, we’re transforming RNA therapeutics by bridging foundational insights with modern innovation,” said Vinod Vathipadiekal, Chief Scientific Officer, Genetic Medicines at Alloy ...

Researchers at the Experimental and Clinical Research Center in Berlin are developing a targeted treatment for muscular dystrophy with the help of gene-editing. Preclinical research led by the Spuler ...

2012; van den Boogaard et al., 2016; Hamanaka et al., 2020). Becker muscular dystrophy (BMD) is an X-linked recessive disorder caused by dystrophin in-frame deletion in the DMD gene. The prevalence of ...